Last update 16 Aug 2025

S-606001

Overview

Basic Info

Drug Type
Small molecule drug
Synonyms
S 606001, S606001
Target
GYS1
Action
inhibitors
Mechanism
GYS1 gene inhibitors
Therapeutic Areas
Nervous System DiseasesCongenital DisordersEndocrinology and Metabolic Disease+ [1]
Active Indication
Glycogen Storage Disease Type II
Inactive Indication-
Originator Organization
Shionogi & Co., Ltd.Shionogi & Co., Ltd.
Active Organization
Shionogi & Co., Ltd.Shionogi & Co., Ltd.
Inactive Organization-
License Organization-
Drug Highest PhasePhase 2
First Approval Date-
Regulation-
Login to view timeline

Related

2
Clinical Trials associated with S-606001
NCT07123155
/ Not yet recruitingPhase 2
A Phase 2, Multicenter, Randomized, Placebo-controlled, Double-blind Study to Investigate the Safety, Pharmacodynamics, and Preliminary Efficacy of S-606001 as an Add-on to Enzyme Replacement Therapy in Patients With Late-onset Pompe Disease
JPRN-jRCT2071240030
/ RecruitingPhase 1IIT
A Phase 1, crossover, open-label study to compare the bioavailability of S-606001 between capsules and tablets and to investigate the food effect with the tablets following a single oral dose in healthy adults aged 18 to 55 years
100 Clinical Results associated with S-606001
Login to view more data
100 Translational Medicine associated with S-606001
Login to view more data
100 Patents (Medical) associated with S-606001
Login to view more data
100 Deals associated with S-606001
Login to view more data

R&D Status

10 top R&D records.
Login
to view more data
IndicationHighest PhaseCountry/LocationOrganizationDate
Glycogen Storage Disease Type IIPhase 2-
Shionogi & Co., Ltd.Shionogi & Co., Ltd.
30 Oct 2025
Login to view more data

Clinical Result

Indication
Phase
Evaluation
View All Results
Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date

No Data

Login to view more data

Translational Medicine

Boost your research with our translational medicine data.
login
or
view full example data
Boost your research with our translational medicine data.

Deal

Boost your decision using our deal data.
login
or
view full example data
Boost your decision using our deal data.

Core Patent

Boost your research with our Core Patent data.
login
or
view full example data
Boost your research with our Core Patent data.

Clinical Trial

Identify the latest clinical trials across global registries.
login
or
view full example data
Identify the latest clinical trials across global registries.

Approval

Accelerate your research with the latest regulatory approval information.
login
or
view full example data
Accelerate your research with the latest regulatory approval information.

Regulation

Understand key drug designations in just a few clicks with Synapse.
login
or
view full example data
Understand key drug designations in just a few clicks with Synapse.
AI Agents Built for Biopharma Breakthroughs
Accelerate discovery. Empower decisions. Transform outcomes.
Get started for free today!
Accelerate Strategic R&D decision making with Synapse, PatSnap’s AI-powered Connected Innovation Intelligence Platform Built for Life Sciences Professionals.
Start your data trial now!
Synapse data is also accessible to external entities via APIs or data packages. Empower better decisions with the latest in pharmaceutical intelligence.
Bio
Bio Sequences Search & Analysis
Sign up for free
Chemical
Chemical Structures Search & Analysis
Sign up for free