Drug Type Small molecule drug |
Synonyms C9orf72 transcriptional modification (Libra Therapeutics) |
Target |
Action modulators |
Mechanism C9orf72 modulators(C9orf72-SMCR8 complex subunit modulators) |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Amyotrophic Lateral Sclerosis | Preclinical | United States | 01 Aug 2025 | |
| Frontotemporal Dementia | Preclinical | United States | 01 Aug 2025 |





