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Last update 07 Jun 2025
Danon disease (Lamp2B)(AskBio)
Last update 07 Jun 2025
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms- |
Target |
Action modulators |
Mechanism LAMP-2 modulators(Lysosome-associated membrane glycoprotein 2 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationOrphan Drug (European Union) |
R&D Status
10 top R&D records. to view more data
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Glycogen Storage Disease Type IIb | Preclinical | United States | 28 Jun 2023 |
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Clinical Result
Clinical Result
Indication
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