Last update 07 Aug 2025

CRISPR/Cas9 and donor DNA-HCAd

Overview

Basic Info

Drug Type
CRISPR/Cas9
Synonyms-
Target
β-glucuronidase
Action
modulators
Mechanism
β-glucuronidase modulators(glucuronidase beta modulators)
Therapeutic Areas
Congenital DisordersEndocrinology and Metabolic DiseaseSkin and Musculoskeletal Diseases+ [1]
Active Indication
Mucopolysaccharidosis VII
Inactive Indication-
Originator Organization
Shaanxi Normal UniversityShaanxi Normal UniversityHenan Medical UniversityHenan Medical University
Active Organization
Shaanxi Normal UniversityShaanxi Normal UniversityHenan Medical UniversityHenan Medical University
Inactive Organization-
License Organization-
Drug Highest PhasePreclinical
First Approval Date-
Regulation-

Related

100 Clinical Results associated with CRISPR/Cas9 and donor DNA-HCAd
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100 Translational Medicine associated with CRISPR/Cas9 and donor DNA-HCAd
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100 Patents (Medical) associated with CRISPR/Cas9 and donor DNA-HCAd
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100 Deals associated with CRISPR/Cas9 and donor DNA-HCAd
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R&D Status

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IndicationHighest PhaseCountry/LocationOrganizationDate
Mucopolysaccharidosis VIIPreclinical
China
Shaanxi Normal UniversityShaanxi Normal University
02 Jul 2025
Mucopolysaccharidosis VIIPreclinical
China
Henan Medical UniversityHenan Medical University
02 Jul 2025
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Clinical Result

Indication
Phase
Evaluation
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Deal

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Approval

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Regulation

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