Betibeglogene autotemcel is a Gene therapy, Hematopoietic stem cell therapy targeting β-globin, at Approved. This 2026 report reviews clinical evidence.
Lovotibeglogene autotemcel is a Gene therapy targeting β-globin, at Approved. This 2026 report reviews clinical evidence, IP, deals, risks and a GO view.
Verdiperstat is a Small molecule drug targeting MPO, at Phase 1. This 2026 report reviews clinical evidence, IP, deals, risks and a HOLD / OPTION view.
Nomacopan is a Recombinant protein targeting C5, at Preclinical. This 2026 report reviews clinical evidence, IP, deals, risks and a HOLD / OPTION view.